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Alternative strategies for F508del-CFTR repair: novel targets for drug discovery approach in Cystic Fibrosis
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Cozza G, Tosco A, Ferrari E, Villella VR, Esposito S, Monzani R, Spinella MC, Venerando A, Rossetto M, Bosello Travain V, Ursini F, Raia V, Maiuri L
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Development of a PI3K?-derived peptide as a novel F508del-CFTR potentiator
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Ghigo A, Murabito A, Ren K, Pirozzi F, Quinney NL, Caldrer S, Sala V, Laudanna C, Melotti P, Gentzsch M, and Hirsch E
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